Healthcare industry consultant and Executive Director for @gene_therapies
Washington, DC
Joined May 2009
- Tweets7.5K
- Following514
- Followers821
- Likes296
Mike Capaldi retweeted
#IGTValues: Family members and #caregivers of #patients with genetic diseases often give up traditional jobs to care for the patient full-time. This tradeoff must be considered & appropriately valued. gene-therapies.org/value-of-…
Mike Capaldi retweeted
The unique nature of #genetherapy means we must think differently about how these transformative treatments are valued. We believe there are several elements to consider in ensuring a holistic & accurate assessment of gene therapies' value. gene-therapies.org/value-of-… (1/11)
Mike Capaldi retweeted
“We recognize that too few individuals are benefitting from or getting access to cancer research breakthroughs… #PatientNav is a key component of that. But we can’t do it alone. We have to do it through partnership.” -ACS & ACS CAN CEO @AmerCancerCEO #CancerNationalForum
Mike Capaldi retweeted
IGT Chairman @ErikPaulsen explains why our work to remove regulatory barriers to access is critical for #GaucherDisease patients & others: “If patients cannot access or afford #genetherapies once approved, the true potential of these therapies will never be fully realized.”
Mike Capaldi retweeted
The first hemophilia A #genetherapy has been approved by the European Commission. For patients who have had limited options, this is a game changer in treatment and an exciting development in the field’s momentum. endpts.com/biomarin-nets-con…
Mike Capaldi retweeted
"These are exciting times & our laws need to keep pace w/ the science. VBPs can & will evolve & if given flexibility now...will ensure that 'how' we pay for innovative treatments will allow for continued innovation in the treatments themselves." - IGT Chairman @ErikPaulsen
Mike Capaldi retweeted
“We are making a difference in people’s lives & that’s a great feeling.” - @Srotberg15, rare disease patient/advocate, avid runner & IGT patient advocate advisory council member shares more about @_OurOdyssey_ & his efforts.
blog.upliftingathletes.org/2… via @UpliftingAth
Mike Capaldi retweeted
#GeneTherapies provide hope for the Duchenne community. @CureDuchenne Senior Director of Advocacy, Erin Frey, explains how the organization is working to fuel hope for Duchenne patients & families: gene-therapies.org/post/pati…
Mike Capaldi retweeted
Rare Disease Leaders Announce Collaboration to Modernize Newborn Screening. To read the full article visit: bit.ly/3hWmyh9 #2020nbs
Mike Capaldi retweeted
Learn more about IGT Patient Advisory Council Member @CureSMA: gene-therapies.org/post/igt-…
Mike Capaldi retweeted
Joshua Ofman, Chief Medical Officer and External Affairs at GRAIL, co-authored an editorial with
@AzraRazaMD
"It is well recognized that improving early cancer detection may be the only way to really put a dent in the cancer mortality curve."
The cancer detection rate—a public health approach to early detection. Guest editorial by @GrailBio's Joshua Ofman & @Columbia's @AzraRazaMD — cancerletter.com/articles/20…
Mike Capaldi retweeted
“Nothing has changed when it comes to the pathway to approval of #genetherapies for diseases w/ unmet need.” @US_FDA's Dr. Marks clarifies the agency's approach following the CRL for Hemophilia A treatment. @jennmcnary shares more here: gene-therapies.org/post/dr-p…
Mike Capaldi retweeted
Thanks to all who joined our webinar today! IGT will continue to host conversations such as this on policy developments in the #genetherapy space. Learn more about #genetherapies, IGT members, & our work at gene-therapies.org
Mike Capaldi retweeted
Join us Monday 7/13 for a conversation on the #CMS proposed rule on value-based purchasing & how it impacts #genetherapy.
gene-therapies.org/post/igt-…
Mike Capaldi retweeted
Dr. Peter Marks, director of the Center for Biologics Evaluation and Research @US_FDA: With gene therapy, we're going from feeding someone a fish for dinner — in the case of taking regular pills — to teaching them how to fish by taking care of them for a lifetime. #AxiosEvents
Mike Capaldi retweeted
"There’s going to be challenges in reimbursing these treatments (#genetherapies)…because they change the paradigm for how we treat disease." - @RealEndpoints EVP/Chief Clinical Officer Dr. Jane Barlow #AxiosEvents
Mike Capaldi retweeted
"This is a chance to get things right once & for all." - @FDACBER's Dr. Marks on the promise of #genetherapies. #AxiosEvents
Mike Capaldi retweeted
"We have to take advantage of all these wonderful, innovative treatments like #genetherapies...we have to think long-term when considering cost-effectiveness." -@RepScottPeters. #AxiosEvents
Mike Capaldi retweeted
MONDAY AT 12:30PM ET: @mikeallen and @bobjherman will discuss the impact of the pandemic on life-saving medical trials and treatments. We’ll hear from @RepScottPeters and @RealEndpoint ’s EVP/Chief Clinical Officer Dr. Jane Barlow. REGISTER: medicalresearchduringacrisis… #AxiosEvents
Mike Capaldi retweeted
IGT Patient Advocacy Advisory Council member and #raredisease advocate @jennmcnary connected w/ @FDACBER Dr. Marks to discuss growing questions around medical research during the pandemic. gene-therapies.org/post/fda-…