gene therapy, genome editing, lentiviral vectors, sickle cell disease, beta-thalassemia, red blood cell, hematopoietic stem cell
Imagine Institute,INSERM,Paris
Joined May 2022
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Miccio lab retweeted
📣Register now for the third webinar of the program “EDITSCD & ERN-EuroBloodNet: Focus on Genetic Therapy for People Living with Sickle Cell Disease.”
Join us to better understand how innovative therapies are moving from lab to clinic!
Register now: eurobloodnet.eu/education-2/…
Miccio lab retweeted
And here it is our last work on Base editing of β0-thalassemia mutations with a nice online cover by Science Translational Medicine!
Thank you to @LabMiccio @Inserm @Imagine Institute and to all our collaborators @marioamendola1
science.org/toc/stm/17/826
This week's issue of #ScienceTranslationalMedicine has arrived!
A transcriptional signature could inform smarter antibiotic use in newborns with sepsis, an approved medication boosts anti-malaria immunity in volunteers, and more. scim.ag/483bUCz
Miccio lab retweeted
This week's issue of #ScienceTranslationalMedicine has arrived!
A transcriptional signature could inform smarter antibiotic use in newborns with sepsis, an approved medication boosts anti-malaria immunity in volunteers, and more. scim.ag/483bUCz
Miccio lab retweeted
With boost to NIH budget, Senate panel rejects Trump’s plan to slash agency | Science | AAAS science.org/content/article/…
Miccio lab retweeted
We're thrilled to be organizing a CRISPR-Cas9 workshop in the beautiful city of Sorrento, featuring renowned scientists from around the globe!
meetings.embo.org/event/25-c…
Miccio lab retweeted
A paralysed man can stand on his own after receiving an injection of neural stem cells to treat his spinal cord injury
go.nature.com/41ZCoRj
Miccio lab retweeted
L’@InstitutImagine est un exemple de réussite à la française dans le domaine de l’innovation en santé.
L’IHU incarne l’excellence.
Excellence dans l’innovation pour mieux comprendre et soigner les maladies rares et génétiques, avec 99 familles brevets actifs,
Excellence dans l’attractivité, comme le démontre l’arrivée à sa tête de Bana Jabri, une professeure en pédiatrie et en immunologie de renommée mondiale.
Pour soutenir et renforcer cette excellence, j’ai annoncé au cours de ma visite que les 3 chaires de Professeur Junior demandées par l’Institut Imagine pour venir en appui de ses chaires d’excellence lui seront bien accordées.
Miccio lab retweeted
🧬 @GeneHumdi COST Action, con la colaboración de @SETGyC, organiza el curso "Optimizing Gene Editing with Advanced Omics: Safety, Off-Target Detection, and Cell Phenotyping", que se celebrará del 11 al 14 de marzo de 2025 en @genyo_pts (Granada, España). ¡Y ofrecen becas! 🧵1/3
Miccio lab retweeted
some heads up,
The @EMBO Workshop "CRISPR-Cas: from biology to therapeutic applications", to be held from 2–5 November 2025 in Sorrento Italy. Please retweet
#CRISPR
Stay tuned for the programe and registration here 👇
coming-soon.embo.org/w25-86
Miccio lab retweeted
𝐍𝐞𝐰 𝐓𝐫𝐢𝐩𝐥𝐞-𝐀𝐜𝐭𝐢𝐨𝐧 𝐂𝐑𝐈𝐒𝐏𝐑 𝐓𝐞𝐜𝐡𝐧𝐨𝐥𝐨𝐠𝐲 𝐄𝐧𝐚𝐛𝐥𝐞𝐬 𝐒𝐢𝐦𝐮𝐥𝐭𝐚𝐧𝐞𝐨𝐮𝐬 𝐆𝐞𝐧𝐞 𝐀𝐜𝐭𝐢𝐯𝐚𝐭𝐢𝐨𝐧, 𝐑𝐞𝐩𝐫𝐞𝐬𝐬𝐢𝐨𝐧, 𝐚𝐧𝐝 𝐃𝐞𝐥𝐞𝐭𝐢𝐨𝐧 𝐢𝐧 𝐏𝐫𝐢𝐦𝐚𝐫𝐲 𝐇𝐮𝐦𝐚𝐧 𝐓 𝐂𝐞𝐥𝐥𝐬
Scientists at Aarhus University have developed a method that allows for simultaneous activation, repression, and knockout of genes within a single cell. By leveraging orthogonal CRISPR/Cas systems, the team, led by Rasmus O. Bak, has demonstrated the potential of advanced CRISPR technologies for innovative applications in gene therapy and regenerative medicine.
Read more in our latest interview with co-first authors of the study, Amalie Dyrelund Broksø and Louise Bidstrup-Bendixen.
✒️ Interview by: Christos Evangelou, PhD, BCMAS
crisprmedicinenews.com/news/…
📸 Photo, from left to right: Simon Bøje Fammé, Louise Bidstrup-Bendixen, Amalie Dyrelund Broksø, and Rasmus O. Bak.
#crisprmedicinenews #crisprmedicine #crispr #geneediting #crispra #crispri #geneticengineering
Miccio lab retweeted
Drs. Giulia Hardouin, Annarita Miccio (@LabMiccio), and @MeganeBrusson review breakthroughs in gene addition- and genome-editing-based therapies for β-thalassemia and more.
Check it out!
bit.ly/40otJ9U
Miccio lab retweeted
Nouvelle publication scientifique ! Importance des études de sécurité et d'efficacité pour le traitement de la drépanocytose par CRISPR-Cas9, pour en savoir plus 👉 institutimagine.org/fr/impor…
Miccio lab retweeted
A new Commentary co-authored with @pshangaris has just been published in Molecular Therapy. It accompanies an important paper published in the same journal by @LabMiccio . To access the Commentary, see link below:
authors.elsevier.com/a/1k7lu…
Miccio lab retweeted
Thanks to all @Genehumdi members volunteering, and congratulations to the #EarlyCareer and #YoungResearchers participating in our #MeetTheExperts during the @ESGCT #Rome2024meeting !!
Miccio lab retweeted
Sammy Basso @SammyBasso, one of the most remarkable people to share our world, passed away last night from complications associated with progeria, the ultra-rare ‘rapid aging’ genetic disease Sammy both suffered from and transcended.
Sammy realized that a base editing treatment that corrects the root cause of progeria and rescues animals with the disease would likely not be ready in time for him, but worked tirelessly every day to bring this potential treatment to other patients so they might have a better life.
Sammy made the most of every day, living with great purpose, intention, and joy that was inspiring, infectious, and reminded us of what’s truly important.
We miss him terribly. 😔
xitter.cf/davidrliu/status/16807…
reuters.com/world/europe/sur…
Miccio lab retweeted
Gene therapy in hemoglobinopathies is a hot topic, so it was great to hear from Annarita Miccio (@LabMiccio) on the challenges associated with this treatment approach & the role it may play in the future.🧬
Keep an eye out on VJHemOnc.com to find out more!
#ASCAT2024 @ascatconference
Miccio lab retweeted
I am thrilled to announce that I have been awarded the prestigious 5-year @ERC_Research #StartingGrant! I still can’t believe it!
Kudos also to my colleagues @o_attya and Irene Franco for their ERCs! New exciting challenges ahead!
@SanRaffaeleMI
@Telethonitalia
Miccio lab retweeted
The European Rare Diseases Research Alliance @ERDERA_org kicks off with a bold vision to make Europe a global leader in rare diseases research and innovation. 🚀
Read press release🗞️erdera.org/wp-content/upload…
🌍💙 #ERDERA #RareDiseases
@EUScienceInnov @HorizonEU @Inserm
Miccio lab retweeted
"France needs to redesign its national science policies. The government should focus less on what research to encourage and more on how to attract and retain researchers. This will foster an environment in which ideas can grow" nature.com/articles/d41586-0…
Miccio lab retweeted
Joint session @EHA_Hematology and @ISEHSociety about #GeneTherapy for #Thalassemia. Giulia Hardouni from @LabMiccio presented #base editing for B thalassemia
