Aggie. Texan. Entrepreneur. ALS Advocate living with ALS.

College Station, TX
Joined May 2017
Craig Reagan retweeted
❤️ I HAVE SOME EXCITING NEWS TO SHARE! I am incredibly honored and excited to announce that I've been selected to speak in person at the FDA's Rare Disease Framework Public Meeting on October 28th in Silver Spring, Maryland! This meeting is especially meaningful because it focuses on the FDA's new initiative and recently released white paper, A New Framework for Rare Disease Review. For someone who has spent so many years advocating for the Huntington's disease community, this opportunity means more to me than I can adequately put into words. I'm not just an advocate. I'm gene-positive, someone living with the reality of a progressive, rare brain disease. I've watched this disease take so much from people I love, and I know firsthand what is at stake when we talk about treatment development, regulatory decisions, and the time patients have left. I've spent nearly two decades fighting for a seat at the table. On October 28th, I'll have the privilege of using that seat to help shape a future where the patient voice is not an afterthought, but a foundation of the process. And that means everything to me. ❤️ The FDA's new Rare Disease Framework Initiative represents an opportunity to rethink how treatments for rare diseases are developed and reviewed, recognizing that rare diseases present unique challenges that traditional approaches don't always adequately address. It's an opportunity to discuss what evidence is realistically attainable, how we can improve consistency and predictability in regulatory decisions, and how patients can have a meaningful role throughout the process. But here's the part I really want everyone to hear: 📣 YOU HAVE A SEAT AT THIS TABLE, TOO! The FDA is inviting public comments on this initiative, and this is an opportunity for patients, caregivers, families, advocates, researchers, and everyone impacted by rare diseases to provide input. You don't need a medical degree. You don't need to understand every detail of regulatory science. 💪Your lived experience IS expertise. And your voice deserves to be heard. 💙 📣 HOW TO GET INVOLVED: 📝 Submit a public comment: regulations.gov/docket/FDA-2… Docket #: FDA-2026-N-12214 📅 Deadline to submit comments: December 11, 2026 📖 Read the FDA's new white paper and learn about the initiative: fda.gov/industry/fda-rare-di… 💻 Learn about the October 28th public meeting and how to attend virtually: fda.gov/news-events/fda-meet… I'm excited. I'm humbled. And I'm incredibly grateful for this opportunity. But more than anything, I'm hopeful about what we can accomplish when patients are genuinely included in shaping the systems that determine our futures. We have an opportunity to make a difference. Let's not waste it. Because for those of us living with progressive rare diseases, every day matters. Disease progression can cause irreversible damage. And what we stand to lose isn't just time - it's our independence, our abilities, precious moments with our families, and the futures we're fighting so hard to protect. ❤️ Time Matters. And so do our voices. #RareDisease #HuntingtonsDisease #FDA #PatientAdvocacy #PatientVoice #TimeMatters #RareDiseaseResearch #RareDiseaseFramework
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Please go to this site and leave comment supporting new rare disease framework and why its vitally important to patients living w/ #ALS, #HUNTINGTONS, #DMD and many others. Its can also an avenue to call them out for intentionally stalling NurOwn! regulations.gov/docket/FDA-2…
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Grateful for @FDA_KyleD's leadership to transform regulatory policy. The #raredisease community desperately needs these regulations to be implemented ASAP. But while we await this multi-year process, we need @FDADrugs to act wth existing regulatory flexibility to get drugs like #NurOwn, #deramiocel and #AMT130 to people with #ALS #Duchenne and #Huntingtons. People are #DyingWaiting. #EndALS #EndHD #EndDMD #EndDuchenne
AEI senior fellow @ScottGottliebMD joins CNBC ‘Squawk Box’ to discuss the FDA’s new Rare Disease Framework Initiative and its guidance for developing drugs for unmet patient needs.
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Oops, I used the wrong handle last time. Lets try this again... @BrainstormCell I have a donor that has committed to pay for my NurOwn treatment through the "Right To Try" act. How does the process work? Who do we contact? I'm ready!! #nurownworks
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Every word of this is, in reality, far worse than you could ever imagine. Come on, FDA, move your ass!! @SecKennedy @FDA_KyleD @realDonaldTrump @SecRollins
#ALS - this terminal illness is physically, mentally and emotionally draining. The grief of not being able to do what your heart wants. The slow loss of independence. Not being able to fulfill dreams. Each day you lose more and more. The uncertainty weighs heavy.
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No child should have to crawl up stairs because his government won't give him access to a cell therapy that could help him retain function. What are you waiting for @FDA? @FDA_KyleD, Karim Mikhail and @FDADrugs please approve @capricor's #deramiocel with the same urgency as you did the pancreatic cancer drug that only extended survival by 6 months. The boys and young men with #Duchenne deserve the same chance at life. #EndDMD #EndDuchenne #rarediseases #MuscularDystrophy @POTUS @SecKennedy @SenRonJohnson @SenRickScott @SenGillibrand @SenateAging @LeaderJohnThune @SenatorWicker @GOPHELP @RandPaul @SenJohnBarrasso @HouseCommerce
I asked Ryu what it is like to live with #Duchenne and this is what he told me.  “At first it was really hard to understand my diagnosis, and some days it’s still really hard. But God helps me with it everyday.”  15 million American children like him are living with a rare disease. So many are waiting for the FDA approved treatments that could extend their lives or ease the symptoms of their disease. @FDA, what are you waiting for? @FDA_KyleD @FDADrugs @SecKennedy @HHSGov @realDonaldTrump
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Apparently, you need to hear this @SecKennedy @FDA_KyleD @realDonaldTrump . While the FDA dicks around w/whether to approve NurOwn for ALS, 40K Americans suffer, along with 1,000's of family members. APPROVE NUROWN NOW! nurownworks.com @MinoShah facebook.com/share/v/1E65BWh…
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Why doesn't the ALS Association ever deliver hope like this? Answer: Because THEY SUCK! They ONLY support drugs/therapies from which they receive financial BENEFIT! facebook.com/share/v/1PR4bSL… @MinoShah @Ml1969 @Vita_Victoria2 @JC75408607 @juan23188549 @SecKennedy @elonmusk
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Craig Reagan retweeted
Hey Senate! Pass ACT for ALS NOW or face our wrath!!! Good night moon.
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A 75% slowing in lethal disease progression is a HUGE WIN! And these changes on the bounded scale are validated by a reduction in objective biomarker NfL. @FDACommissioner @FDA_KyleD @FDADrugs Listen to the people who know #Huntingtons best -- the expert neurologists and patients who have watched generations of their families die. Use the regulatory flexibility that Congress mandated and grant accelerated approval of @uniQure_NV's AMT130 as these changes are "reasonably likely to predict a clinically meaningful benefit." #EndHD $QURE #neurology #MedTwitter #NeuroTwitter #DyingWaiting
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Such a no brainer that @FDA must listen to the specialists who know the disease the best. Hoping @FDA_KyleD and next @FDACommissioner continue to defer to the experts as they did for Replimune approval decision. People with ALS, #Huntingtons, #ataxia, #Sanfilippo, #Duchenne and so many other #rarediseases deserve the same expertise and same humanity as extended to cancer patients. Thanks to author, @MinoShah, a @HopkinsMedicine educated anesthesiologist who has been battling #ALS for 15 years. He's seen so many broken promises by the @FDADrugs.
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.@ChrisJohnson28, assigning @MyronRolle as a strategic advisor to the @NFLPA is ONLY something Myron will put on his resume. @JCTretter @ReevesMaybin know this. I pray you direct them to get @FDADrugs @FDA_KyleD @FDA @SecKennedy @RobertKennedyJr to give a damn about #ALS The Danger to NFL Players: YOU inspired this! NFL players are supporting you, unaware they could be next. There is 4X THE RISK for players, while the public's #ALS lifetime risk is 1 out of every 300 people & is becoming more common (expected to increase at least 40% in the next decade). A Broken System: Every new @FDAadministration & Congress give EMPTY PROMISES to a new generation of dying #ALS patients, but we're forgotten the second we walk out. They have 0 ACCOUNTABILITY, because we ALL DIE! I've emailed #FDA leadership & Congress directly thinking that, as a physician who now faces a 100% FATAL death sentence, they might listen when I explain that the @FDACRUEL regulatory rigidity for ALS is not only cruel for the people who are dying now, but it prevents R&D into future treatments from pharmaceutical companies. I WAS WRONG. The Call to Action: NFL players going to the #FDA & Congress are things the media and the FDA/Congress can't ignore. If @FDAdrugs gave a damn about #ALS, you would be getting effective NUROWN, instead of the #FDACBER being nearly 8 months past its own deadline for responding to our NUROWN Citizens Petition. @realDonaldTrump @DrOz @DrOzCMS @RepGuthrie @RepAndyHarrisMD @PatMcAfeeShow @DeionSanders @AdrianPeterson @MoneyLynch @DeSeanJackson10 @CutonDime25 @AaronDonald97 @markingramII @camjordan94 @VonMiller @CrosbyMaxx @JeromeBettis36 @D_Hest23 @AndrewWhitworth @DBrooks55 @REALPACMAN24 @thereal_lendale @VinceYoung10 @EdgerrinJames @JCTretter @ReevesMaybin @JJWatt @Ochocinco @ShannonSharpe
With profound sadness, we mourn the passing of our beloved O.J. Brigance following his extraordinary and heroic battle with ALS.
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Very few people do I respect less than @VPrasadMDMPH. He has no integrity. It's an awful trait for an @FDADrugs director. People die. Vinayak lied to the public with the ease & arrogance of a sociopath. He was the @FDA's grim reaper. There's a lot of blood on his hands, but I don't expect a sociopath to care.
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Very few people do I respect less than @VPrasadMDMPH. He has no integrity. It's an awful trait for an @FDADrugs director. People die. Vinayak lied to the public with the ease & arrogance of a sociopath. He was the @FDA's grim reaper. There's a lot of blood on his hands. I don't expect a sociopath to care.
.@VPrasadMDMPH sits down for the first time since leaving the Trump administration’s @FDA The WSJ called him the FDA’s Grim Reaper, he says it’s dishonest. This week we talk about why. He talks to @Getthecheckpod about Moderna’s shares skyrocketing 170%, what the public doesn’t understand about rare disease drugs, and if he identifies as right wing (the answer might surprise you). 00:00 Introducing Vinay Prasad, the FDA's former vaccine chief 04:19 Vinay’s words are moving public markets (a few times!) 10:25 Society weighing education years vs COVID deaths 12:49 How do you run experiments mid-epidemic 17:32 Do masks work 23:38 The ethics of a medical study 26:34 Does Vinay believe in vaccines 37:58 Can a parent say no to cancer treatment for their child 41:27 Lobbyist money in FDA decisions 49:31 What's the FDA's conflict of interest 49:58 Vinay's controversies: WSJ calls him the grim reaper 53:13 The former FDA vaccine chief on @Kalshi’s clinical trial markets 01:00:08 Why is American healthcare so broken 01:01:19 Peptides 01:05:10 Who do patient advocacy groups represent 01:08:49 Vinay supports universal healthcare?!
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