
Lab of Dr. Stephanie Cherqui @UCSDHealth. Developing stem cell and gene therapy strategies for degenerative multi-systemic disorders.
La Jolla, California
Joined October 2022
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Cherqui Lab retweeted
@CIRMnews is a proud sponsor of the Gene Therapy Initiative Symposium at @UCSDHealth, which bring together researchers and industry experts to share scientific discoveries and boost collaboration to advance cell and gene therapy treatments for patients everywhere. #gtiUCSD
Cherqui Lab retweeted
Check out this report from @CherquiLab et al. "Rescue of Alzheimer's disease phenotype in a mouse model by transplantation of wild-type hematopoietic stem and progenitor cells", published in @CellReports #ASGCT2024 hubs.li/Q02wFqBN0
Come checkout our Postdoc Veenita’s poster on Renal Fanconi Sundrome in Cystinosis @WORLDSymposia
Cherqui Lab retweeted
Excited to kick off @WORLDSymposia lysosomal disease conference this year by attending an important @CureSanfilippoF meeting on leveraging data to advance Sanfilippo therapeutic development! #lysosomes #genetherapy #hspc #sanfilippo #mps @UCSDHealth @MPSSociety
We are thrilled for our project scientist Anusha to be 1 of 10 researchers receiving a $20,000 grant from @UpliftingAth! This grant will aid her research and support the 1 in 10 Americans diagnosed with a #RareDisease. upliftingathletes.org/2024/0…
Cherqui Lab retweeted
Excited to be at the @MPSSociety 37th Annual Family Conference to present some of my work at @CherquiLab on gene modified HSPC for MPSIIIC! @UCSDHealth #GeneTherapy #StemCells
Backed by a $5M gift from Nancy & Geoffrey Stack Foundation, @UCSanDiego officially launches the Gene Therapy Initiative 🧬. Led by Drs. Cherqui & Muotri, the initiative will fuel research🔬+ gene therapies💉to benefit patients with #Genetics disorders
today.ucsd.edu/story/uc-san-…
Cherqui Lab retweeted
Out now in @CellReports, Dr. Stephanie Cherqui's (@Cherqui_S) lab shows hematopoietic #StemCell transplants can protect against memory loss, neuroinflammation and β-amyloid build-up in a mouse model of #AlzheimersDisease 🧠
today.ucsd.edu/story/stem-ce…
Cherqui Lab retweeted
EXCITING STUDY! In new proof-of-concept study, Priyanka Mishra, Stephanie Cherqui et al. show #StemCell transplants may also be promising therapeutic against #AlzheimersDisease. @CherquiLab @ucsdstemcell @ljiresearch @CellReports
doi.org/10.1016/j.celrep.202…
today.ucsd.edu/story/stem-ce…
Cherqui Lab retweeted
Honoured to have been awarded one of the @ASGCTherapy 2023 outstanding poster award for my abstract on my work in the @CherquiLab @UCSDHealth on Hematopoeitic #stemcell #genetherapy for MPSIIIC funded by @MPSSociety & @CureSanfilippoF
Great week for the Cherqui lab @ASGCTherapy presenting our latest work! #stemcell #genetherapy @UCSDHealth linkedin.com/posts/stephanie…
Cherqui Lab retweeted
Happy to be back presenting a poster at the @ASGCTherapy annual meeting on my work at @CherquiLab on #stemcell #GeneTherapy for Sanfilippo C funded by @MPSSociety & @CureSanfilippoF. Poster No. 649
Cherqui Lab retweeted
🎧 NEW PODCAST 🎧 Professor @Cherqui_S is a pioneer in the field of #CRISPR cell and gene therapies. She speaks about her work on curing genetic diseases such as Friedreich's ataxia, obstacles in clinical development, and the future of CRISPR therapies 👉 hubs.li/Q01HM8kb0
Thank you @rafaelabadell for representing our lab at @WORLDSymposia 2023. Also, a special acknowledgement goes out to @MPSSociety and @CureSanfilippoF for your fellowship supports!
Cherqui Lab retweeted
I am very happy and grateful to have received the fellowship award from the @CureSanfilippoF to continue my work investigating the use of #stemcell #genetherapy to treat Sanfilippo type C in the @CherquiLab @UCSDHealth
Excited to share the FAID reel of 2022! It's a delightful visual summary of our recent conference. Our team has worked hard to make this event happen, and we couldn't be more proud of what we have achieved so far. #ClinicalTrials #GeneTherapy
france-science.com/en/france…
Cherqui Lab retweeted
Congratulations to all of the recipients, including @AquilanoKatia, @Cherqui_S, and @USFHealth
Together, we will #SlowStopReverse and #CureFA
Cherqui Lab retweeted
Professor Stephanie Cherqui of @UCSDMedSchool speaks to us about a prestigious grant from the California Institute for Regenerative Medicine, which will allow her team to bring a new CRISPR therapy for Friedreich’s ataxia to the clinic.
Read more here: bit.ly/3WxA2nV

ALT Stephanie Cherqui Ph.D is an Associate Professor in the Department of Paediatrics, Division of Genetics at the University of California San Diego. Her team is developing therapeutic strategies based on gene-edited haematopoietic stem and progenitor cell transplantation to treat Friedreich’s ataxia and other multi-systemic degenerative disorders. Photo courtesy of Stephanie Cherqui
















